2c304433dc59aa72b9a57635a3781448.ppt
- Количество слайдов: 37
Integrating NGS approaches into patient care: How I manage high-risk disease at presentation in a transplant eligible patient Prof Chng Wee Joo Director National University Cancer Institute, Singapore (NCIS) Research National University Health System (NUHS) Deputy Director Clinical Care Cancer Science Institute, Singapore (CSI) National University of Singapore (NUS) Education
Disclosure • Employment – NA • Stock Ownership – NA • Honoraria – Janssen, Novartis, Celgene, Roche • Research Funding – Roche, Celgene • Advisory Board – Janssen, Novartis, Celgene, Roche
Outline • Clinical Utility of NGS • How do we identify high risk MM • Implication on Treatment
Companion Diagnostics in MM Landgren and Morgan CCR 2014
Key Pathways RAS/MAPK NFKB DNA Damage Epigenetic Lohr et al. Cancer Cell 2014; 25: 91 -101
Prognosis JCO 2015
Novel Drug Targets
Cancer Discovery 2013; 3: 862 -869
Myeloma is clonally heterogenous
Slide Courtesy of Dr Rafael Fonseca
Gaps for NGS • Driver vs passenger • Lack of standardisation (Depth, panel, algorithm) • How to handle mutations of unknown significance • How to prioritize mutations
How to identify the High-Risk Patients Definition: Median survival of 2 years (Chng et al Leukemia 2015)
Revised ISS Palumbo et al JCO 2015
Evolution of Prognostic System ISS + FISH + GEP
Combination of ISS with GEP Kuiper et al. Blood 2015
Prognostic Signatures • UAMS 70 -gene signature (Shaughnessy JD et al. Blood 2007; 109: 2276 -2284) • IFM signature (Decaux O et al. J Clin Oncol 2008; 26: 4798 -805) • Centrosome Index (Chng WJ et al. Blood 2006; 107: 3669 -3675; Chng WJ et al. Blood 2008; 111: 1603 -1609) • IL 6 -HMCL signature (Moreaux J et al. Haematologica 2011; 96: 574 -82) • HZD Cell Death signature (Dickens NJ et al. Clin Cancer Res 2010; 16: 1856 -64) • CINGEC signature (Chung TH et al. PLo. S ONE 2013; 8: e 66361)
Combination of Signature Chng et al, Leukemia 2016
Chng et al, Leukemia 2016
ISS-MUT Factors ISS CNSA – t(4; 14), 17 p(del), MYC Translocation, 1 q+ Mut - TP 53, ZFHX 4, CCND 1, ATM and ATR Group 1 – ISS I or II, no CNSA or Mut Group 2 – ISS III, no CNSA or Mut or ISS I/II/III + 1 CNSA/Mut Group 3 – 2 CNSA or Mut, regards of ISS
Summary of Prognostic Factors Pre-treatment Post-treatment Host Age Albumin Tumor Burden Beta-2 microglobulin PET-CT Tumor Biology Genetics Response Early Relapse
Can novel agents modulate risk?
Weinhold et al Leukemia 2015
Shaughnesy et al. Br J Haematol 2009; 147: 347 -351
What About the Newer Agents Pomalidomide Dimopoulos et al. Haematologica 2015
Ixazomib - Tourmaline ORR, % IRd ≥VGPR, % Placebo -Rd IRd 78. 3* 71. 5 Standard-risk patients 80 All high-risk patients ≥CR, % Placebo -Rd IRd 48. 1* 39 73 51 79* 60 Patients with del(17 p)† 72 Patients with t(4; 14) alone 89 All patients Median PFS, months Placebo -Rd IRd Placebo -Rd HR 11. 7* 6. 6 20. 6 14. 7 0. 742* 44 12 7 20. 6 15. 6 0. 640* 45* 21 12* 2 21. 4 9. 7 0. 543 48 39 15 11* 0 21. 4 9. 7 0. 596 76 53 28 14 4 18. 5 12. 0 0. 645 Moreau ASH 2015
Carfilzomib - Endeavour Chng ASH 2015
What have we learn • Velcade especially benefit t(4; 14) patients • Inclusion of Velcade (and hence prolonged use) in different phases of treatment is important in high-risk disease • The use of double autologous transplant seem to also be an important factor. • Revlimid seem to have a more moderate and less consistent effect on high-risk disease • Thalidomide maintenance contra-indicated in 17 p 13 deletion • Newer Imids and PI may be more effective
Conclusion • No current routine role for NGS in clinic yet • We should adopt standardized risk categories Ø Revised ISS should be current gold standard Ø GEP and post-treatment MRD/Imaging await further studies • No evidence for the routine application of risk-adapted therapy Ø Best evidence is use of Velcade for patients with t(4; 14) • Should incorporate risk stratification into design of clinical trials Ø Test hypothesis in high-risk patients e. g. Velcade maintenance, double transplant, allo-SCT, Use of novel PI and Imids upfront
Thank You - Questions Research Clinical Care Education